The delivery challenge: fulfilling the promise of therapeutic genome editing
Joost van Haasteren, Jie Li, Olivia J. Scheideler, Niren Murthy, David V. Schaffer
Topics & Concepts
Genome editingComputational biologyImmunogenicityCRISPRGenomeGenetic enhancementGene deliveryBiologyNucleaseGenome engineeringViral vectorGeneGeneticsRecombinant DNAImmune systemCRISPR and Genetic EngineeringVirus-based gene therapy researchRNA Interference and Gene Delivery