Litcius/Paper detail

The 10th Oligonucleotide Therapy Approved: Golodirsen for Duchenne Muscular Dystrophy

Annemieke Aartsma‐Rus, David R. Corey

2020Nucleic Acid Therapeutics133 citationsDOIOpen Access PDF

Topics & Concepts

Duchenne muscular dystrophyMedicineInternal medicineCRISPR and Genetic EngineeringPluripotent Stem Cells ResearchRetinal Development and Disorders