Givosiran in acute intermittent porphyria: A personalized medicine approach
Antoine Poli, Caroline Schmitt, Boualem Moulouel, Arienne Mirmiran, Neila Talbi, Sophie Rivière, Diane Cerutti, Isabelle Bouchoule, Anthony Faivre, Vincent Grobost, Claire Douillard, F. Duchêne, Valeria Fiorentino, Thierry Dupré, Hana Manceau, Katell Peoc’h, Hervé Puy, Thibaud Lefèbvre, Laurent Gouya
Topics & Concepts
Acute intermittent porphyriaAdverse effectMedicineContext (archaeology)NauseaInternal medicinePorphyriaDosingPaleontologyBiologyPorphyrin Metabolism and DisordersFolate and B Vitamins ResearchPhotodynamic Therapy Research Studies