Nusinersen for Patients With Spinal Muscular Atrophy: 1415 Doses via an Interdisciplinary Institutional Approach
Elena Madan, Sabrina Carrié, Carolina Donado, Kimberly Lobo, Michelle Souris, Regina Laine, Elizabeth Beers, Laura Cornelissen, Basil T. Darras, Anjali Koka, Bobbie Riley, Pradeep Dinakar, Scellig Stone, Brian D. Snyder, Robert J. Graham, Horacio M. Padua, Navil F. Sethna, Charles B. Berde
Topics & Concepts
MedicineSpinal muscular atrophySacrumSpinal deformitySMA*Spinal fusionFluoroscopyUnivariate analysisLumbarSurgeryScoliosisPhysical therapyMultivariate analysisInternal medicineDiseaseCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchCraniofacial Disorders and Treatments