Death after High-Dose rAAV9 Gene Therapy in a Patient with Duchenne’s Muscular Dystrophy
Angela Lek
Topics & Concepts
MedicineDuchenne muscular dystrophyMuscular dystrophyGenetic enhancementPediatricsGeneInternal medicineGeneticsBiologyVirus-based gene therapy researchCAR-T cell therapy researchCRISPR and Genetic Engineering