Comparison of Longitudinal Outcomes in Children with Primary Ciliary Dyskinesia and Cystic Fibrosis
BreAnna Kinghorn, Margaret Rosenfeld, Erin Sullivan, Frankline Onchiri, Marshall Brown, Rhonda D. Szczesniak, Thomas Ferkol, Scott D. Sagel, Sharon Dell, Carlos Milla, Adam J. Shapiro, Kelli M. Sullivan, Maimoona A. Zariwala, Jessica E. Pittman, Michael R. Knowles, Stephanie D. Davis, Margaret W. Leigh
Abstract
In childhood, average lung function abnormalities in PCD are not milder than CF, particularly for those with IDA/MTD ciliary defects. New guidelines and treatments to improve outcomes in PCD are urgently needed.
Topics & Concepts
Primary ciliary dyskinesiaMedicineCystic fibrosisDyskinesiaPediatricsInternal medicineBronchiectasisLungDiseaseParkinson's diseaseCystic Fibrosis Research AdvancesPediatric health and respiratory diseases