Engineered mischarged transfer RNAs for correcting pathogenic missense mutations
Yichen Hou, Wen Zhang, Philip T. McGilvray, Marek Sobczyk, Tianxin Wang, Shao Huan Samuel Weng, Allen Huff, Sihao Huang, Noah Peña, Christopher D. Katanski, Tao Pan
Topics & Concepts
Missense mutationTransfer RNANonsense mutationBiologyGeneticsMutantGenePoint mutationMutationRNATranslation (biology)Computational biologyMessenger RNARNA and protein synthesis mechanismsRNA modifications and cancerRNA Interference and Gene Delivery