Morpholino oligonucleotide-mediated exon skipping for DMD treatment: Past insights, present challenges and future perspectives
Shalini Gupta, Swrajit Nath Sharma, Jayanta Kundu, Sankha Pattanayak, Surajit Sinha
Topics & Concepts
Exon skippingMorpholinoDuchenne muscular dystrophyDystrophinExonAntisense therapyOligonucleotideBioinformaticsMedicineComputational biologyBiologyGeneticsGene knockdownAlternative splicingGeneLocked nucleic acidRNA Interference and Gene DeliveryAdvanced biosensing and bioanalysis techniquesMuscle Physiology and Disorders