Characterization and AAV-mediated CRB gene augmentation in human-derived CRB1KO and CRB1KOCRB2+/− retinal organoids
Nanda Boon, Xuefei Lu, Charlotte A. Andriessen, M A Orlova, Peter M. J. Quinn, Camiel J. F. Boon, Jan Wijnholds
Abstract
-associated retinal dystrophies.
Topics & Concepts
RetinalBiologyRetinitis pigmentosaOrganoidRetinaPhenotypeElectroretinographyCell biologyRetinal DisorderRetinal degenerationGeneticsGeneNeuroscienceBiochemistryRetinal Development and DisordersRetinal Diseases and TreatmentsRetinal and Macular Surgery