Litcius/Paper detail

Optimization of TAM16, a Benzofuran That Inhibits the Thioesterase Activity of Pks13; Evaluation toward a Preclinical Candidate for a Novel Antituberculosis Clinical Target

Caroline Wilson, Peter C. Ray, Fabio Zuccotto, Jorge Hernández, Anup Aggarwal, Claire J. Mackenzie, Nicola Caldwell, Malcolm Taylor, Margaret Huggett, Michael Mathieson, Dinakaran Murugesan, Alasdair Smith, Susan H. Davis, Mattia Cocco, Maloy Kumar Parai, Arjun Acharya, Fábio K. Tamaki, Paul Scullion, Ola Epemolu, Jennifer Riley, Laste Stojanovski, Eva María López-Román, Pedro Alfonso Torres-Gómez, Ana Maria Toledo, Laura Guijarro-López, Isabel Camino, Curtis A. Engelhart, Dirk Schnappinger, Lisa M. Massoudi, Anne J. Lenaerts, Gregory T. Robertson, Chris Walpole, David J. Matthews, David Floyd, James C. Sacchettini, Kevin D. Read, Lourdes Encinas, Robert H. Bates, Simon R. Green, Paul G. Wyatt

2021Journal of Medicinal Chemistry35 citationsDOIOpen Access PDF

Abstract

, its main liability was inhibition of the hERG cardiac ion channel. This article describes the optimization of the series toward a preclinical candidate. Despite improvements in the hERG liability in vitro, when new compounds were assessed in ex vivo cardiotoxicity models, they still induced cardiac irregularities. Further series development was stopped because of concerns around an insufficient safety window. However, the demonstration of in vivo activity for multiple series members further validates Pks13 as an attractive novel target for antitubercular drugs and supports development of alternative chemotypes.

Topics & Concepts

hERGBenzofuranPharmacologyMycobacterium tuberculosisChemistryCardiotoxicityIn vivoTuberculosisDrug discoveryComputational biologyMedicineBiochemistryPotassium channelBiologyBiotechnologyToxicityStereochemistryInternal medicinePathologyOrganic chemistryTuberculosis Research and EpidemiologyComputational Drug Discovery MethodsCancer therapeutics and mechanisms