Litcius/Paper detail

The CD22-IGF2R interaction is a therapeutic target for microglial lysosome dysfunction in Niemann-Pick type C

John V. Pluvinage, Jerry Sun, Christel Claes, Ryan A. Flynn, Michael S. Haney, Tal Iram, Xiang-Ling Meng, Rachel Chanel Lindemann, Nicholas M. Riley, Emma Danhash, Jean Paul Chadarevian, Emma Tapp, David Gate, Sravani Kondapavulur, Inma Cobos, Sundari Chetty, Anca M. Pașca, Sergiu P. Pașca, Elizabeth Berry‐Kravis, Carolyn R. Bertozzi, Mathew Blurton‐Jones, Tony Wyss‐Coray

2021Science Translational Medicine39 citationsDOIOpen Access PDF

Abstract

mutant induced pluripotent stem cell–derived microglia-like cells without harming oligodendrocytes in vitro. These findings reinforce the differences between mouse and human microglia and provide a candidate microglia-directed immunotherapeutic to treat NPC.

Topics & Concepts

LysosomeMedicineNeuroscienceChemistryBiologyBiochemistryEnzymeLysosomal Storage Disorders ResearchAutoimmune and Inflammatory Disorders ResearchCytomegalovirus and herpesvirus research