Autologous gene therapy for hemoglobinopathies: From bench to patient’s bedside
Franco Locatelli, Marina Cavazzana, Haydar Frangoul, Josu de la Fuente, Mattia Algeri, Roland Meisel
Topics & Concepts
Bench to bedsideGenetic enhancementMedicineIntensive care medicineBiologyGeneMedical physicsGeneticsCRISPR and Genetic EngineeringVirus-based gene therapy researchInnovation and Socioeconomic Development