Hematopoietic Stem Cell-Targeted Gene-Addition and Gene-Editing Strategies for β-hemoglobinopathies
Claire Drysdale, Tina Nassehi, Jackson Gamer, Morgan Yapundich, John F. Tisdale, Naoya Uchida
Topics & Concepts
BiologyGeneGenome editingHaematopoiesisStem cellGeneticsHematopoietic stem cellComputational biologyCellCRISPRBioinformaticsCRISPR and Genetic EngineeringHemoglobinopathies and Related DisordersSARS-CoV-2 and COVID-19 Research