Litcius/Paper detail

BCL11A +58/+55 enhancer-editing facilitates HSPC engraftment and HbF induction in rhesus macaques conditioned with a CD45 antibody-drug conjugate

Selami Demirci, Jing Zeng, Rahul Palchaudhuri, Chuanfeng Wu, Diana M. Abraham, Taha Bartu Hayal, Khaled Essawi, My Anh Nguyen, Ulana Stasula, Rebecca Chu, Alexis Leonard, Shaina N. Porter, Muhammad Behroz Naeem Khan, Gabriela Hinojosa, Naoya Uchida, Sogun Hong, Cícera R. Lazzarotto, Nola Neri, Lucas Ferreira da Silva, Danilo Pellin, Archana Verma, Leanne Lanieri, Anjali Bhat, Katelyn J. Hammond, Tiffany Tate, Stacy A. Maitland, Fatemeh Sheikhsaran, Aylin Bonifacino, Allen E. Krouse, Nathaniel S. Linde, Theresa Engels, Justin Golomb, Shengdar Q. Tsai, Shondra M. Pruett‐Miller, David T. Scadden, Cynthia E. Dunbar, Scot A. Wolfe, Robert E. Donahue, Lisa Olson, Daniel E. Bauer, John F. Tisdale

2024Cell stem cell16 citationsDOI

Topics & Concepts

BiologyEnhancerConjugateAntibody-drug conjugateAntibodyDrugCell biologyImmunologyPharmacologyCancer researchMolecular biologyMonoclonal antibodyGeneticsTranscription factorGeneMathematicsMathematical analysisErythrocyte Function and PathophysiologyBlood groups and transfusionHemoglobinopathies and Related Disorders