Emerging therapies for Duchenne muscular dystrophy
Theodora Markati, Maryam Oskoui, Michelle A. Farrar, Tina Duong, Nathalie Goemans, Laurent Servais
Topics & Concepts
Duchenne muscular dystrophyClinical trialDystrophinExon skippingMuscular dystrophyMedicineBioinformaticsDiseaseAdverse effectInternal medicineExonBiologyGeneGeneticsAlternative splicingMuscle Physiology and DisordersCardiomyopathy and Myosin StudiesTissue Engineering and Regenerative Medicine