Drug Repurposing for Rare Diseases
Helen I. Roessler, Nine Knoers, Mieke M. van Haelst, Gijs van Haaften
Topics & Concepts
Drug repositioningRepurposingDrugDrug developmentOrphan drugMedicineIntensive care medicinePopulationPharmacologyBioinformaticsBiologyEnvironmental healthEcologyCRISPR and Genetic EngineeringGenomics and Rare DiseasesBiochemical and Molecular Research