Re: “Moving Forward After Two Deaths in a Gene Therapy Trial of Myotubular Myopathy” by Wilson and Flotte
Perry B. Shieh, Carsten G. Bönnemann, Wolfgang Müller‐Felber, Astrid Blaschek, James J. Dowling, Nancy L. Kuntz, A. Seferian
Topics & Concepts
Genetic enhancementMyopathyMedicineGeneticsBiologyGeneInternal medicineGenomics and Rare DiseasesNeurological disorders and treatmentsGenetic Neurodegenerative Diseases