Homology-directed repair of an MYBPC3 gene mutation in a rat model of hypertrophic cardiomyopathy
Jiali Nie, Yu Han, Zhiyuan Jin, Weijian Hang, Hongyang Shu, Wen Zheng, Li Ni, Dao Wen Wang
Topics & Concepts
Hypertrophic cardiomyopathyCRISPRGenome editingBiologyCas9MutationGeneticsPhenotypeGeneCardiomyopathyMedicineInternal medicineHeart failureBiochemistryCardiomyopathy and Myosin StudiesCRISPR and Genetic EngineeringCongenital heart defects research