Litcius/Paper detail

Base-edited cynomolgus monkeys mimic core symptoms of STXBP1 encephalopathy

Zongyang Lu, Siting He, Jian Jiang, Ling Zhuang, Yan Wang, Guang Yang, Xiaoyu Jiang, Yanhong Nie, Jiqiang Fu, Xiaotong Zhang, Yong Lu, Xinyan Bian, Hung-Chun Chang, Zhi‐Qi Xiong, Xingxu Huang, Zhen Liu, Qiang Sun

2022Molecular Therapy17 citationsDOIOpen Access PDF

Topics & Concepts

BiologyEncephalopathyBioinformaticsNeuroscienceGeneticsMedicineInternal medicineCellular transport and secretionRetinal Development and DisordersNeuroscience and Neuropharmacology Research