Towards a treatment for genetic prion disease: trials and biomarkers
Sonia M. Vallabh, Eric Vallabh Minikel, Stuart L. Schreiber, Eric S. Lander
Topics & Concepts
DiseaseClinical trialMedicinePrion proteinBioinformaticsIntensive care medicineBiologyPathologyPrion Diseases and Protein MisfoldingNeurological diseases and metabolismNuclear Receptors and Signaling