Litcius/Paper detail

Malate dehydrogenase 2 deficiency is an emerging cause of pediatric epileptic encephalopathy with a recognizable biochemical signature

Jessica Priestley, Lisa M. Pace, Kuntal Sen, Anjali Aggarwal, Cesar Alves, Ian M. Campbell, Sanmati Cuddapah, Nicole Engelhardt, Marina Eskandar, Paloma C. Jolín García, Andrea Gropman, Ingo Helbig, Xinying Hong, Vykuntaraju K. Gowda, Laina Lusk, Pamela Trapane, Varunvenkat M. Srinivasan, Pim Suwannarat, Rebecca Ganetzky

2022Molecular Genetics and Metabolism Reports21 citationsDOIOpen Access PDF

Abstract

variants.

Topics & Concepts

Malate dehydrogenaseCitrate synthaseBiologyCitric acid cycleEncephalopathyMitochondrionEndocrinologyInternal medicineBiochemistryMedicineEnzymeMetabolismMitochondrial Function and PathologyMetabolism and Genetic DisordersEpilepsy research and treatment