Molecular evaluation and vector integration analysis of HCC complicating AAV gene therapy for hemophilia B
Manfred Schmidt, Graham R. Foster, Michiel Coppens, Hauke Thomsen, Ricardo Dolmetsch, Liesbeth Heijink, Paul E. Monahan, Steven W. Pipe
Topics & Concepts
Genetic enhancementVector (molecular biology)MedicineGeneVirologyBiologyGeneticsRecombinant DNAVirus-based gene therapy researchViral Infectious Diseases and Gene Expression in InsectsRNA Interference and Gene Delivery