Litcius/Paper detail

Efficacy and safety of setmelanotide, a melanocortin-4 receptor agonist, in patients with Bardet-Biedl syndrome and Alström syndrome: a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial with an open-label period

Andrea M. Haqq, Wendy K. Chung, Hélène Dollfus, Robert Haws, Gabriel Ángel Martos‐Moreno, Christine Poitou, Jack A. Yanovski, Robert S. Mittleman, Guojun Yuan, Elizabeth Forsythe, Karine Clément, Jesús Argente

2022The Lancet Diabetes & Endocrinology182 citationsDOIOpen Access PDF

Topics & Concepts

MedicinePlaceboPediatricsInternal medicineClinical endpointRandomized controlled trialClinical trialAlternative medicinePathologyGenetic and Kidney Cyst DiseasesGenetic Syndromes and ImprintingRegulation of Appetite and Obesity