Efficacy and safety of setmelanotide, a melanocortin-4 receptor agonist, in patients with Bardet-Biedl syndrome and Alström syndrome: a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial with an open-label period
Andrea M. Haqq, Wendy K. Chung, Hélène Dollfus, Robert Haws, Gabriel Ángel Martos‐Moreno, Christine Poitou, Jack A. Yanovski, Robert S. Mittleman, Guojun Yuan, Elizabeth Forsythe, Karine Clément, Jesús Argente
Topics & Concepts
MedicinePlaceboPediatricsInternal medicineClinical endpointRandomized controlled trialClinical trialAlternative medicinePathologyGenetic and Kidney Cyst DiseasesGenetic Syndromes and ImprintingRegulation of Appetite and Obesity