Age and baseline values predict 12 and 24-month functional changes in type 2 SMA
Giorgia Coratti, Maria Carmela Pera, Simona Lucibello, Jacqueline Montes, Amy Pasternak, Anna Mayhew, Allan M. Glanzman, Sally Dunaway Young, Marika Pane, Mariacristina Scoto, Sonia Messina, Nathalie Goemans, Andres Nascimiento Osorio, Marina Pedemonte, Valeria Sansone, Enrico Bertini, Darryl C. De Vivo, Richard S. Finkel, Francesco Muntoni, Eugenio Mercuri
Topics & Concepts
SMA*MedicineCohortSpinal muscular atrophyRetrospective cohort studyInternal medicineDiseaseCombinatoricsMathematicsNeurogenetic and Muscular Disorders ResearchCardiac Structural Anomalies and RepairMechanical Circulatory Support Devices