Calmodulin inhibitors improve erythropoiesis in Diamond-Blackfan anemia
Alison M. Taylor, Elizabeth R. Macari, Iris T. Chan, Megan C. Blair, Sergei Doulatov, Linda T. Vo, David M. Raiser, Kavitha Siva, Anindita Basak, Mehdi Pirouz, Arish N Shah, Katherine McGrath, Jessica M. Humphries, Emma Stillman, Blanche P. Alter, Eliezer Calo, Richard I. Gregory, Vijay G. Sankaran, Johan Flygare, Benjamin L. Ebert, Yi Zhou, George Q. Daley, Leonard I. Zon
Abstract
cells isolated from a patient with DBA. This work uncovers a potential avenue of therapeutic development for patients with DBA.
Topics & Concepts
Diamond–Blackfan anemiaErythropoiesisCalmodulinAnemiaIneffective erythropoiesisMedicinePhenotypeBiologyInternal medicineGeneticsCalciumGeneRNARibosomeRNA modifications and cancerCancer-related gene regulationEpigenetics and DNA Methylation