Litcius/Paper detail

Efficacy and safety of the neonatal Fc receptor inhibitor efgartigimod in adults with primary immune thrombocytopenia (ADVANCE IV): a multicentre, randomised, placebo-controlled, phase 3 trial

Catherine M. Broome, Vickie McDonald, Yoshitaka Miyakawa, Monica Carpenedo, David J. Kuter, Hanny Al‐Samkari, James B. Bussel, Marie Godar, Jaume Ayguasanosa, Kristof De Beuf, Francesco Rodeghiero, Marc Michel, Adrian C. Newland, Michael Fillitz, Paul Knoebl, Stef Meers, Ismail Amine, Jaromír Gumulec, Antonín Hluší, Jiřı́ Mayer, Philippe Quittet, Jean‐François Viallard, M Betaneli, I Datikashvili-David, Genadi Iosava, Levan Makhaldiani, László Rejtő, Nino Sharashenidze, Stefanie Groepper, Alexander Röth, Aryan Hamed, Árpád Illés, Monica Carpenedo, Andrea Artoni, Monica Bocchia, Barbara Gamberi, Alessandra Borchiellini, Esther Natalie Olíva, Andrea Patriarca, Simona Tomassetti, Yoshitaka Miyakawa, Kiyoshi Ando, Hiroshi Handa, Shinya Katsutani, Kaichi Nishiwaki, Shoko Ito, Tomoki� Ito, Fransien de Boer, A.J. Gerard Jansen, Hanna Ciepłuch, Szymon Fornagiel, Sebastian Grosicki, Maria Soroka‐Wojtaszko, Jacek Treliński, Б. А. Бакиров, Elena Borisenkova, Elena Volodicheva, Yuri Shatokhin, Andrey Proydakov, Maria Aranzazu Alonso, María Eva Mingot‐Castellano, Blanca Sánchez‐González, Blanca Sanchez-Gonzalez, Meltem Aylı, Tuba Hacıbekiroğlu, Ahmet Muzaffer Demir, Meliha Nalçacı, Mehmet Sönmez, Anıl Tombak, Selami Koçak Toprak, Burhan Turgut, Filiz Vural, Münci Yağcı, Fevzi Altuntaş, Mehmet Turgut, Emın Kaya, Nataliya Romanyuk, Vickie McDonald, Syed Rashid Saeed Kazmi, Catherine M. Broome, Spero R. Cataland, Ketan Doshi, Steven R. Lentz, Michael Boxer, Richard Rosenberg, Michael Boxer, Richard Rosenberg

2023The Lancet91 citationsDOIOpen Access PDF

Topics & Concepts

MedicineClinical endpointPlaceboImmune thrombocytopeniaInternal medicineAutoantibodyAdverse effectPopulationPlateletIntention-to-treat analysisDosingImmune systemGastroenterologyRandomized controlled trialAntibodyImmunologyPathologyEnvironmental healthAlternative medicinePlatelet Disorders and TreatmentsMonoclonal and Polyclonal Antibodies ResearchAutoimmune Bullous Skin Diseases