Health-related quality of life following valoctocogene roxaparvovec gene therapy for severe hemophilia A in the phase 3 trial GENEr8-1

Brian O’Mahony, Amy L. Dunn, Andrew D. Leavitt, Flora Peyvandi, Margareth C. Ozelo, Johnny Mahlangu, Kathelijne Peerlinck, Jiaan‐Der Wang, Gillian Lowe, Chee-Wee Tan, Adam Giermasz, Huyen Tran, Teh‐Liane Khoo, Erin Cockrell, Dominic Pepperell, Hérvè Chambost, María Fernanda López Fernández, Rashid Kazmi, Elaine M. Majerus, Mark W. Skinner, Robert Klamroth, Jennifer Quinn, Hua Yu, Wing Yen Wong, Tara M. Robinson, Steven W. Pipe