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Synaptopodin deficiency exacerbates kidney disease in a mouse model of Alport syndrome

Liang Ning, Hani Suleiman, Jeffrey H. Miner

2021American Journal of Physiology-Renal Physiology22 citationsDOIOpen Access PDF

Abstract

Alport syndrome (AS) is a hereditary disease of the glomerular basement with hematuria and proteinuria. Podocytes eventually exhibit foot process effacement, indicating actin cytoskeletal changes. To investigate how cytoskeletal changes impact podocytes, we generated Alport mice lacking synaptopodin, an actin-binding protein in foot processes. Analysis showed a more rapid disease progression, demonstrating that synaptopodin is protective. This suggests that the actin cytoskeleton is a target for therapy in AS and perhaps other glomerular diseases.

Topics & Concepts

Alport syndromePodocyteSynaptopodinGlomerular basement membraneGlomerulonephritisGlomerulosclerosisAlbuminuriaPodocinBiologyKidneyKidney diseaseEndocrinologyInternal medicineNephropathyPathologyProteinuriaMedicineDiabetes mellitusRenal Diseases and GlomerulopathiesChronic Kidney Disease and DiabetesCell Adhesion Molecules Research
Synaptopodin deficiency exacerbates kidney disease in a mouse model of Alport syndrome | Litcius