Risdiplam for Prenatal Therapy of Spinal Muscular Atrophy
Richard S. Finkel, Samuel H. Hughes, J. W. Parker, Matthew Civitello, Alfonso Lavado, Heather C. Mefford, Lutz Mueller, Heidemarie Kletzl
Topics & Concepts
Spinal muscular atrophyMedicineAtrophyPhysical medicine and rehabilitationPathologyDiseaseNeurogenetic and Muscular Disorders ResearchCongenital Anomalies and Fetal SurgeryCardiac Structural Anomalies and Repair