Litcius/Paper detail

State of Gene Therapy for Monogenic Cardiovascular Diseases

Sahej Bains, John R. Giudicessi, Katja E. Odening, Michael J. Ackerman

2024Mayo Clinic Proceedings12 citationsDOIOpen Access PDF

Topics & Concepts

Genetic enhancementMedicineModalitiesGene silencingGeneBioinformaticsViral vectorVector (molecular biology)Intensive care medicineGeneticsBiologyRecombinant DNASocial scienceSociologyCRISPR and Genetic EngineeringCardiomyopathy and Myosin StudiesViral Infections and Immunology Research