Inotersen for the Treatment of Hereditary Transthyretin Amyloidosis
Maria Mahfouz, Rika Maruyama, Toshifumi Yokota
Topics & Concepts
TransthyretinAmyloidosisPolyneuropathyMedicineCardiomyopathyInternal medicinePharmacologyHeart failureAmyloidosis: Diagnosis, Treatment, OutcomesProtein Kinase Regulation and GTPase SignalingPeptidase Inhibition and Analysis