Molecular mechanisms of the ambroxol action in Gaucher disease and GBA1 mutation-associated Parkinson disease
Zuzanna Cyske, Lidia Gaffke, Estera Rintz, Karolina Wiśniewska, Grzegorz Węgrzyn, Karolina Pierzynowska
Topics & Concepts
AmbroxolParkinson's diseaseDiseaseGlucocerebrosidaseMutationMedicineDegenerative diseaseNeurosciencePharmacologyGeneticsBiologyInternal medicinePsychiatryGeneLysosomal Storage Disorders ResearchParkinson's Disease Mechanisms and TreatmentsCellular transport and secretion