Editing Approaches to Treat Alpha-1 Antitrypsin Deficiency
Derek M. Erion, L. Liu, Christopher R. Brown, Stephen I. Rennard, Humam Farah
Topics & Concepts
Alpha 1-antitrypsin deficiencyAlpha (finance)MedicineInternal medicineSurgeryPatient satisfactionConstruct validityRNA regulation and diseaseProtease and Inhibitor MechanismsLysosomal Storage Disorders Research