Gene-based therapies for neurodegenerative diseases
Jichao Sun, Subhojit Roy
Topics & Concepts
Genetic enhancementNeuroscienceDiseaseSpinal muscular atrophyViral vectorMedicineBioinformaticsNeurodegenerationGeneBiologyPathologyGeneticsRecombinant DNANeurogenetic and Muscular Disorders ResearchCRISPR and Genetic EngineeringGenetics and Neurodevelopmental Disorders