Long-term efficacy of nusinersen and its evaluation in adolescent and adult patients with spinal muscular atrophy types 1 and 2
Hideyuki Iwayama, Kohei Kawahara, Mizuki Takagi, Shingo Numoto, Yoshiteru Azuma, Hirokazu Kurahashi, Yumiko Yasue, Hiroyuki Kawajiri, Atsushi Yanase, Teruyoshi Ito, Shinya Kimura, Toshiyuki Kumagai, Akihisa Okumura
Topics & Concepts
SMA*MedicineSpinal muscular atrophyPediatricsPhysical therapySurgeryInternal medicineCombinatoricsMathematicsDiseaseNeurogenetic and Muscular Disorders ResearchCraniofacial Disorders and TreatmentsSpinal Dysraphism and Malformations