Voxelotor in adolescents and adults with sickle cell disease (HOPE): long-term follow-up results of an international, randomised, double-blind, placebo-controlled, phase 3 trial
Jo Howard, Kenneth I. Ataga, Robert C. Brown, Maureen Achebe, Videlis Nduba, Amal El‐Beshlawy, Hoda Hassab, Irene Agodoa, Margaret Tonda, Sarah Gray, Joshua Lehrer‐Graiwer, Elliott Vichinsky
Topics & Concepts
MedicinePlaceboClinical trialPediatricsSickle cell anemiaDiseaseInternal medicineAlternative medicinePathologyHemoglobinopathies and Related DisordersBlood groups and transfusionIron Metabolism and Disorders