Litcius/Paper detail

iPSC-derived neural precursor cells engineering GBA1 recovers acid β-glucosidase deficiency and diminishes α-synuclein and neuropathology

Yanyan Peng, Benjamin Liou, Yi Lin, Christopher N. Mayhew, Sheila M. Fleming, Ying Sun

2023Molecular Therapy — Methods & Clinical Development13 citationsDOIOpen Access PDF

Abstract

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Topics & Concepts

NeuropathologyNeurodegenerationNeural stem cellSubstantia nigraBiologyNeuroinflammationAlpha-synucleinCell biologyChemistryCancer researchStem cellParkinson's diseaseImmunologyPathologyMedicineDiseaseInflammationLysosomal Storage Disorders ResearchCellular transport and secretionRetinal Development and Disorders