Spinal Muscular Atrophy Treatments, Newborn Screening, and the Creation of a Neurogenetics Urgency
Russell J. Butterfield
Topics & Concepts
Spinal muscular atrophySMA*NeurogeneticsMedicineFood and drug administrationAtrophyDiseaseSMN1Physical medicine and rehabilitationIntensive care medicinePathologyPharmacologyMathematicsCombinatoricsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery