Litcius/Paper detail

A precision gene-engineered B cell medicine producing sustained levels of active factor IX for hemophilia B therapy

Hanlan Liu, Swati Singh, Timothy Mullen, Caroline Bullock, Sean Keegan, Troy Patterson, Sakshisingh Thakur, Amy Lundberg, Sol Shenker, Ryan Couto, Charuta Yadav, Shamael R. Dastagir, Lily Li, Wayne Bainter, Ella Liberzon, C D Malloy, Cícera R. Lazzarotto, Toshiro K. Ohsumi, Shalini Chilakala, Huei-Mei Chen, Rashmi Kshirsagar, Anja Hohmann, Sean P. Arlauckas, Adam S. Lazorchak, Christopher M. Scull, Richard A. Morgan

2025Molecular Therapy5 citationsDOIOpen Access PDF

Topics & Concepts

Factor IXGenetic enhancementMedicineCancer researchGeneBiologyComputational biologyImmunologyInternal medicineGeneticsHemophilia Treatment and ResearchCAR-T cell therapy researchHepatitis B Virus Studies