In vivo base editing rescues primary hyperoxaluria type 1 in rats
Zhoutong Chen, D. Zhang, Rui Zheng, Lei Yang, Yanan Huo, Dan Zhang, Xiaoliang Fang, Yueyan Li, Guofeng Xu, Dali Li, Hongquan Geng
Topics & Concepts
Primary hyperoxaluriaIn vivoBase (topology)Primary (astronomy)Type (biology)MedicineInternal medicineEndocrinologyKidneyBiologyGeneticsMathematicsAstronomyPhysicsEcologyMathematical analysisBiomedical Research and PathophysiologyOrgan Donation and TransplantationPorphyrin Metabolism and Disorders