CRISPR/Cas9–mediated metabolic pathway reprogramming in a novel humanized rat model ameliorates primary hyperoxaluria type 1
Rui Zheng, Yueyan Li, Liren Wang, Xiaoliang Fang, Junqi Zhang, Lei He, Lei Yang, Dali Li, Hongquan Geng
Topics & Concepts
CRISPRReprogrammingBiologyPrimary hyperoxaluriaMedicineGeneticsKidneyGeneKidney Stones and Urolithiasis TreatmentsBiomedical Research and PathophysiologyTissue Engineering and Regenerative Medicine