Sirolimus Can Increase the Disappearance Rate of Cardiac Rhabdomyomas Associated with Tuberous Sclerosis: A Prospective Cohort and Self-Controlled Case Series Study
Xiao-Qiao Chen, Yangyang Wang, Mengna Zhang, Qian Lu, Ling-Yu Pang, Liying Liu, Yufen Li, Li‐Ping Zou
Topics & Concepts
Tuberous sclerosisSirolimusProspective cohort studyMedicineCohortSeries (stratigraphy)Cohort studyPediatricsInternal medicineCardiologyRadiologyBiologyPaleontologyTuberous Sclerosis Complex ResearchPI3K/AKT/mTOR signaling in cancerTumors and Oncological Cases