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Large Language Models for Rare Disease Diagnosis at the Undiagnosed Diseases Network

Cathy Shyr, Thomas Cassini, Rory J. Tinker, Kevin Byram, Peter J. Embí, Lisa Bastarache, Josh F. Peterson, Hua Xu, Rizwan Hamid, Undiagnosed Diseases Network

2025JAMA Network Open12 citationsDOIOpen Access PDF

Abstract

This cohort study assesses whether large language models (LLMs) can identify the final diagnosis, based on available clinical information, for patients referred to the Undiagnosed Diseases Network.

Topics & Concepts

CohortDiseaseMedicineIntensive care medicineRare diseasePediatricsPathologyArtificial Intelligence in Healthcare and EducationGenomics and Rare DiseasesMachine Learning in Healthcare
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