Antisense oligonucleotide jacifusen for FUS-ALS: an investigator-initiated, multicentre, open-label case series
Neil A. Shneider, Matthew B. Harms, Vladislav A. Korobeynikov, Olivia M. Rifai, Benjamin N. Hoover, Elizabeth A. Harrington, Sonya Aziz‐Zaman, Jessica Singleton, Arish Jamil, Vikram Madan, Julia Yasek, Ik Jae Lee, Jinsy Andrews, Richard M Smiley, Mahabub M Alam, L. Black, Minwook Shin, Jonathan K. Watts, David Walk, Daniel Newman, Robert M. Pascuzzi, Markus Weber, Christoph Neuwirth, Sandrine Da Cruz, Armand Soriano, Roger Lane, Scott P. Henry, Joel Mathews, Paymaan Jafar‐Nejad, Dan Norris, Frank Rigo, Robert H. Brown, Stephan Miller, Rebecca Crean, C. Frank Bennett
Topics & Concepts
Series (stratigraphy)Open labelMedicineBiologyInternal medicineClinical trialPaleontologyAmyotrophic Lateral Sclerosis ResearchNeurogenetic and Muscular Disorders ResearchMitochondrial Function and Pathology