Mechanism-Based Personalized Medicine for Cystic Fibrosis by Suppressing Pseudo Exon Inclusion
Saiko Shibata, Masahiko Ajiro, Masatoshi Hagiwara
Topics & Concepts
ExonRNA splicingCystic fibrosis transmembrane conductance regulatorCystic fibrosisAlternative splicingMinigeneMutationBiologyPhosphorylationCancer researchGeneGeneticsCell biologyChemistryRNACystic Fibrosis Research AdvancesNeurogenetic and Muscular Disorders ResearchNeonatal Respiratory Health Research