Potential disease-modifying therapies for Huntington's disease: lessons learned and future opportunities
Sarah J. Tabrizi, Carlos Estevez‐Fraga, Willeke van Roon‐Mom, Michael Flower, Rachael I. Scahill, Edward J. Wild, Ignacio Muñoz-Sanjuán, Cristina Sampaio, Anne Rosser, Blair R. Leavitt
Topics & Concepts
HuntingtinHuntington's diseaseDiseaseHuntingtin ProteinTrinucleotide repeat expansionBiologyRNA splicingBioinformaticsGeneticsGeneMedicineRNAInternal medicineAlleleGenetic Neurodegenerative DiseasesMitochondrial Function and PathologyNeurological disorders and treatments