The UBE3A-ATS antisense oligonucleotide rugonersen in children with Angelman syndrome: a phase 1 trial

Joerg F. Hipp, Carlos A. Bacino, Lynne M. Bird, Ina Bruenig-Traebert, Daniel Chan, Marie‐Claire Y. de Wit, Paulo Fontoura, G. H. S. Hooper, Ravi Jagasia, Michelle L. Krishnan, L. Murtagh, Alessandro Noci, Ana Roche Martínez, Dietmar Schwab, Mercedes Serrano, Mark D. Shen, Julian Tillmann, Jorrit Tjeertes, Brenda Vincenzi, Elizabeth Berry‐Kravis, Azad Bonni, the Rugonersen Study Group, Muhamed Barakovic, Charlotte Bon, Ponghatai Boonsimma, Mariana Bustamante, Katalin Buzasi, Stormy Chamberlain, Susanne Clinch, Siobhan Connor-Ahmad, Philipp Daetwyler, Oana Danila, Sebastian Holst, Thomas Kremer, Florian Lipsmeier, Stefano Magon, Amanda Messer, David Nobbs, Giuseppe Palermo, Lisa Squassante, Thomas Wiese, all TANGELO investigators, Jennifer M. Bain, Jamie Capal, Ralitza Gavrilova, María Muñoz Cabeza, Nicola Pietrafusa, Rajsekar Rajamaran, Shafali Jeste, Federico Vigevano