Real-world respiratory and bulbar comorbidities of SMA type 1 children treated with nusinersen: 2-Year single centre Australian experience
Kerrie‐Anne Chen, John Widger, Arthur Teng, Dominic A. Fitzgerald, Arlene D’Silva, Michelle A. Farrar
Topics & Concepts
MedicinePediatricsCohortRespiratory systemMechanical ventilationGastrostomyObservational studySurgeryInternal medicineNeurogenetic and Muscular Disorders ResearchAmyotrophic Lateral Sclerosis ResearchHereditary Neurological Disorders