Nusinersen in Adults with 5q Spinal Muscular Atrophy: a Systematic Review and Meta-analysis
Maria Gavriilaki, Maria Moschou, Vasileios Papaliagkas, Konstantinos Notas, Evangelia Chatzikyriakou, Sotirios Papagiannopoulos, Marianthi Arnaoutoglou, Vasilios Κ. Kimiskidis
Topics & Concepts
MedicineMeta-analysisSpinal muscular atrophySMA*Observational studySubgroup analysisPopulationAdverse effectPediatricsCochrane LibraryInternal medicineMEDLINEPhysical therapyPolitical scienceDiseaseEnvironmental healthMathematicsLawCombinatoricsNeurogenetic and Muscular Disorders ResearchRNA modifications and cancerCongenital Anomalies and Fetal Surgery