Litcius/Paper detail

A pause in gene therapy: Reflecting on the unique challenges of sickle cell disease

Alexis Leonard, John F. Tisdale

2021Molecular Therapy39 citationsDOIOpen Access PDF

Topics & Concepts

Genetic enhancementDiseaseCellCell therapyGeneMedicineBiologyComputational biologyBioinformaticsGeneticsInternal medicineHemoglobinopathies and Related DisordersParvovirus B19 Infection StudiesPrenatal Screening and Diagnostics